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Quantitative microdialysis Cytoskeleton Myostatin DMSXL mice Exercice Antisense oligonucleotide ARN CRISPR/Cas9 Mouse models Myotonic dystrophy mouse models PacBio RNA interference In vivo Brain Genotype phenotype correlation Heart failure Trinucleotide Repeat Expansion DMPK Dystrophie myotonique Myotonic Dystrophy type 1 Exercise Heart Cell model Myotonic Dystrophy Type 1 Aging Alternative splicing Myotonic dystrophy Gene editing Acetylcholinesterase knockout mouse Dilated cardiomyopathy Myotonic dystrophy type 1 Hypoxia GABA Cell culture model Desmin Motoneuron Maximal force Intermediate filament Mouse model Knockout AAV RNA splicing Cardiac muscle Astrocytes CONGENITAL MYATHENIC SYNDROME CTG repeat contractions Acetylcholinesterase deficiency RNA biology MBNL Transgenic mouse model Muscular dystrophy Glucocorticoids Autophagy Mice Lc3 ACETYLCHOLINESTERASE Dynamin 2 Duchenne muscular dystrophy KNOCKOUT MICE Centronuclear myopathy CMS Glucocorticoid-receptor Acute coronary syndrome Expression DM1 Skeletal muscle Dystrophin Antisense oligonucleotides Transgenic mouse Oligodendrocyte Myelin BIOLOGIE MOLECULAIRE Oligodendrocytes Muscle CTG repeats Central nervous system Gene therapy Humans Dystrophie Myotonique Animals Thérapie génique GSK3␤ CRISPRi Gene Therapy Glutamate Myotonic Dystrophy Brain dysfunction PCR Neuron Diaphragm Long read sequencing Therapy Trinucleotide repeat expansion Cell penetrating peptide Astrocyte Fibrosis Male Glial cells CTG repeat instability Transcriptomics